![Susannah greeting Dr. Jennifer Bain, a pediatric neurologist at NewYork-Presbyterian Morgan Stanley Children’s Hospital in Manhattan, who infused Susannah’s drug into her spine.](https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_200_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=i9voGT4P 200w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_260_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=HNmC7wTt 260w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_320_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=SaQ1DWnf 320w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_400_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=bwS0ZvKN 400w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_520_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=UM-1b3eC 520w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_640_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=Ggg1F2o9 640w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_800_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=xGel7GSH 800w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_1040_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=4SOEK8A_ 1040w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_1280_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=6M-Tl07q 1280w, https://www.neurology.columbia.edu/sites/default/files/styles/cola_media_1600_21_9/public/media/images/2022-12/credit-nyt-dr.bain_.jpg?itok=65uOJec7 1600w)
They Created a Drug for Susannah. What About Millions of Other Patients?
December 20, 2022
Susannah Rosen, 8, spent much of her childhood in hospitals in New York City as doctors documented the gradual loss of her ability to stand, walk and see.
But on a visit this October [to Dr. Jennifer Bain, a pediatric neurologist at NewYork-Presbyterian Morgan Stanley Children’s Hospital in Manhattan], her parents thought for the first time that she might leave the hospital better off than before. That’s when surgeons infused a drug into her spine to fix the ultrarare genetic glitch that had vexed her nervous system since infancy. [read more]
Source: The New York Times